The Hereditary Neuropathy Foundation (HNF), an advocacy and research 501c3 non-profit, today...
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Courtney
DTx Pharma Receives FDA Orphan Drug Designation for DTx-1252 for the Treatment of Charcot-Marie-Tooth Disease Type 1A (CMT1A)
Dtx today announced that the FDA has granted Orphan Drug Designation to DTx-1252, an investigational FALCON small interfering RNA (siRNA) therapeutic for the treatment of Charcot-Marie-Tooth Disease Type 1A (CMT1A).
Great News From HNF TRIAD Industry Partner — Pharnext
Pharnext announces new positive results from the ongoing open-label extension study of their drug PXT3003
Great News From HNF TRIAD Industry Partner — Applied Therapeutics
Applied Therapeutics, Inc. has announced that their drug candidate, AT-007 (Govorestat), has received orphan medicinal product designation
Using Medical Cannabis for Managing Pain in Charcot-Marie-Tooth Disease — Patient Reported Outcomes
Data regarding medical cannabis use for pain relief in CMT from HNF’s CMT Patient Registry, GRIN
9 Key Findings from Your GRIN Surveys (and why you need to come back and complete more)
The study highlights the significant impact of neuropathic pain on the quality of life and psychosocial well-being of individuals with CMT.
HNF sheds Light & Research Funding on Mitochondrial Diseases Linked to CMT
Mitochondria are the powerhouses of our cells. Think of them as our body’s batteries. Mitochondrial disease causes these batteries to run low.
HNF Recibió 2023 Health Equity en RARE Impact Grant
¡La Fundación de Neuropatía Hereditaria se complace en anunciar que hemos recibido la Beca de...
CMT Research Update: Pediatric Ankle And Gait Function
HNF TRIAD Academic Partner Connecticut Children’s Publishes Results of CMT Pediatric Natural...
HNF Awarded 2023 Health Equity in RARE Impact Grant
HNF Awarded 2023 Health Equity in RARE Impact Grant For Spanish CMT PSA Awareness Campaign with Diagnosis & Patient Care Toolkit. The Hereditary Neuropathy Foundation is thrilled to announce that we are a recipient of the Global Genes Health Equity in RARE Impact Grant!
Cambridge-led natural history study identifies MTRFR/C12orf65 deficiency to improve diagnosis and therapy development
This research will potentially show a method that may be quicker and better at identifying...
Hereditary Neuropathy Foundation Re-Launches One-of-A-Kind Patient Registry for Charcot-Marie-Tooth Disease Research
Hereditary Neuropathy Foundation Re-Launches One-of-A-Kind Patient Registry for...
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Faces of CMT – Jaxson (7)
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Cannabis (8)
Caregivers (3)
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Pediatrics & CMT (10)
Registry (16)
Research (96)
School Outreach Program and Team CMT Kids (1)
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Bike New York (19)
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TCS New York City Marathon (7)
Team CMT Members (61)
The CMT Genie (6)
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University of San Antonio Texas (1)
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Applied Therapeutics (10)
Pharnext (10)
Rarebase (4)
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CMT Type – CMT1A (22)
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CMT Type – HDAC6 (1)
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CMT Type – SORD Deficiency (9)
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